PPMD’s Duchenne Professionals Masterclass Agenda
We are pleased to offer ten stand-alone courses to allow the professional to create a customized curriculum meeting the learner's unique educational needs, spanning from new-to-Duchenne professionals to seasoned experts in the field.
Participants are eligible to receive continuing education credit upon successful completion of each course — please see individual courses for more information.
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Course 1: Introduction to Duchenne Muscular Dystrophy

- Module 1: The Basics of Duchenne
Edward Smith, MD
Duke Children’s Hospital
- Module 2: The Role of Modifying Genetics in Genotype-Phenotype Correlation
Stanley Nelson, MD
UCLA
- Module 3: Carrier Care - Testing and Management of Female
Dystrophinopathy
Kevin Flanigan, MD
Nationwide Children’s Hospital
- Module 4: Why Multi-Disciplinary Pediatric Care is So Critical
Wendy Chouteau, DNP, APRN, FNP-BC
Cincinnati Children’s Hospital Medical Center
- Module 5: The Key to Successful Transition
Christina Trout, RN, MSN
University of Iowa
- Module 6: The PPMD Certified Duchenne Care
Center Program
Rachel Schrader, MS, APRN, CPNP-PC
Parent Project Muscular Dystrophy
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this live activity for a maximum of 3.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 3.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.3 CEUs for this program.
Course 2: Subspecialty Care Considerations

- Module 1: Duchenne Care Considerations
Mena Scavina, DO
Nemours/Alfred I. duPont Hospital for Children
- Module 2: Cardiac Care
Linda Cripe, MD
Nationwide Children’s Hospital
- Module 3: Pulmonary Care
Rich Kravitz, MD
Duke Children’s Hospital
- Module 4: Endocrinology Care – Bone Health
Leanne Ward, MD, FRCPC
University of Ottawa
- Module 5: Endocrinology Care – Growth and Puberty
Rob Benjamin, MD
Duke Children’s Hospital
- Module 6: Gastrointestinal and Nutrition Care
Kent Williams, MD
Nationwide Children’s Hospital
- Module 7: Psychosocial Care
Seth Sorensen, PhD
Arkansas Children’s Hospital
- Module 8: Physical and Occupational Therapy Considerations
Claudia Senesac, PT, PhD, PCS
University of Florida
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 3.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 3.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.3 CEUs for this program.
Course 3: Demystifying Duchenne Data Collection

- Module 1: MD STARnet Overview
Emma Ciafaloni, MD
University of Rochester
- Module 2: The Duchenne Registry
Ann Martin, MS, CGC
Parent Project Muscular Dystrophy
- Module 3: Creative Solutions for Sharing Data
Mary Schroth
CureSMA
- Module 4: Duchenne Outcomes Research Interchange
David Voccola
Prometheus Research
Ryan Fischer
Parent Project Muscular Dystrophy
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 1.25 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.25 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program
Course 4: Emerging Therapeutics

- Module 1: Animal Models – What They Mean and What
They Don’t
Dominic Wells, PhD
Royal Veterinary College, London
- Module 2: Current Research Strategies – Basic Science
Lee Sweeney, PhD
University of Florida
- Module 3: Current Research Strategies – In the Clinic
Craig McDonald, MD
UC Davis
- Module 4: The Platform Trial
Jane Larkindale, DPhil
Critical Path Institute
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 2.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 2.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.2 CEUs for this program.
Course 5: Accessing Care and Approved Therapies

- Module 1: Access and Reimbursement
Ryan Fischer
Parent Project Muscular Dystrophy
- Module 2: Equitable Access to Clinical Trials and
Approved Therapies
Alison Bateman-House, MPH, PhD
NYU
- Module 3: Equitable Access to Care – Lessons Learned from
the MS Project
Pat Furlong
Parent Project Muscular Dystrophy
- Module 4: The Regulatory Process Explained
Tim Franson, MD
Faegre Drinker Consulting
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 1.75 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.75 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.
Course 6: About Parent Project Muscular Dystrophy (PPMD)

- Module 1: Historical Perspectives of Duchenne Legislation
Pat Furlong
Parent Project Muscular Dystrophy
- Module 2: Resources and Community Education
Amanda Wilkison, RN, BSN
Parent Project Muscular Dystrophy
- Module 3: Engaging with the Community
Nicole Herring
Parent Project Muscular Dystrophy
- Module 4: Partnering with the Community to Drive
Drug Development
Eric Camino, PhD
Parent Project Muscular Dystrophy
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 1.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.
Course 7: Viral Based Therapies

- Module 1: Viral Therapy Basics – Serotypes and
Production Approaches
Jim Wilson, MD, PhD
UPenn
- Module 2: Immune Issues – Innate and Acquired,
and How to Treat
Tim Cripe, MD, PhD, FAAP
Nationwide Children’s Hospital
- Module 3: Durability of Viral Therapies Over Time
Lee Sweeney, PhD
Parent Project Muscular Dystrophy
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this internet enduring activity for a maximum of 1.5 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.5 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.
Course 8: Lessons Learned from Gene Therapy

- From Testing to Treatment: Immunity Explained
Jerry Mendell, MD
Nationwide Children’s Hospital
- Experiences in Gene Therapy:
Having Hard Conversations
Edward Smith, MD
Duke Children’s Hospital
- Panel Discussion: What Would You Tell a Center
About to Embark on Gene Therapy?
Moderator: Pat Furlong
Parent Project Muscular Dystrophy
Jerry Mendell, MD
Nationwide Children’s Hospital
Edward Smith, MD
Duke Children’s Hospital
Russell Butterfield, MD, PhD
University of Utah
Perry Shieh, MD, PhD
UCLA
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this live activity for a maximum of 1.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.
Course 9: Navigating Informed Consent and Screen Fails

- The Nature of Truly Informed Consent
Kevin Flanigan, MD
Nationwide Children’s Hospital
- Counseling Families Through Fear and Failure:
A Conversation about Screen Fails
Colleen Labbadia
Parent, Florida
Kevin Flanigan, MD
Nationwide Children’s Hospital
Erica Goude, MS, CCRP
UC Davis
- Resiliency: Caring for Ourselves, So We Can Care for
Our Patients
Brandon Kozar, PsyD, MBA
Nationwide Children’s Hospital
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this live activity for a maximum of 1.25 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.25 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.
Course 10: Crisis Management – Lessons Learned from the COVID-19 Pandemic

- Duchenne and COVID-19 Incidence and Outcomes: Is Duchenne a Risk Factor?
Jeffery Auletta, MD
Nationwide Children’s Hospital
- Implementation of Telehealth: Success and
Opportunities for Growth
Oren Kupfer, MD
Children’s Hospital Colorado
- Crisis Planning: How to Prepare for the Next
“Big One” with Innovative Solutions
Sue Apkon, MD
Children’s Hospital Colorado
- Question & Answer
Moderator: Rachel Schrader, MS, APRN, CPNP-PC
Parent Project Muscular Dystrophy
Category 1: Duke University Health System Department of Clinical Education and Professional Development designates this live activity for a maximum of 1.0 AMA Category 1 Credit(s)TM. Physicians should claim only credit commensurate with the extent of their participation in the activity.
Nurse CE: Duke University Health System Department of Clinical Education and Professional Development designates this activity for up to 1.0 credit hours for nurses. Nurses should claim only credit commensurate with the extent of their participation in this activity.
IACET: Duke University Health System Clinical Education and Professional is authorized by IACET to offer 0.1 CEUs for this program.

In support of improving patient care, the Duke University Health System Department of Clinical Education and Professional Development is accredited by the American Nurses Credentialing Center (ANCC), the Accreditation Council for Pharmacy Education (ACPE), and the Accreditation Council for Continuing Medical Education (ACCME), to provide continuing education for the health care team.

Duke University Health System Clinical Education and Professional is accredited by the International Association for Continuing Education and Training (IACET) and is authorized to issue the IACET CEU.